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Boy with SPG50, an Ultra-Rare Disease begins Groundbreaking Gene Therapy Clinical Trial
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SPG50
Rare Disease
Fundraising
Alex's Lemonade Stand Foundation Helps Child with Neuroblastoma Find Clinical Trial
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Neuroblastoma
Fundraising
Cancer
n-Lorem Foundation Provides Experimental Medicine to Child With Ultra Rare Disease KIF1A
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Rare Disease
KIF1A
Fundraising
Principal Investigator from Leiden Discusses the Role of Seed Funding for Research on Langerhans Cell Histiocytosis
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Rare Disease
Histiocytosis
Fundraising
MIT Economist Dr. Andrew Lo Discusses New Models For Understanding Clinical Trials Finance and Success
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Fundraising
Data Science
Clinical Trials
Drug Repurposing for Rare Disease from RareBeacon
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Rare Disease
Fundraising
AI
Fundraiser for Clinical Studies of KCNC1
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Rare Disease
KCNC1
Fundraising
1st Annual Scramble for SYNGAP1 Clinical Trials
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SynGAP
Rare Disease
Fundraising
FSHD Clinical Trials in Australia
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Rare Disease
Fundraising
FHSD
Ice Bucket Challenge Funds ALS Clinical Trials
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Fundraising
ALS
Rare Disease PMD Clinical Trials
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Rare Disease
Fundraising
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