Boy with SPG50, an Ultra-Rare Disease begins Groundbreaking Gene Therapy Clinical Trial

Alex's Lemonade Stand Foundation Helps Child with Neuroblastoma Find Clinical Trial

n-Lorem Foundation Provides Experimental Medicine to Child With Ultra Rare Disease KIF1A

Principal Investigator from Leiden Discusses the Role of Seed Funding for Research on Langerhans Cell Histiocytosis

MIT Economist Dr. Andrew Lo Discusses New Models For Understanding Clinical Trials Finance and Success

Drug Repurposing for Rare Disease from RareBeacon

Fundraiser for Clinical Studies of KCNC1

1st Annual Scramble for SYNGAP1 Clinical Trials

FSHD Clinical Trials in Australia

Ice Bucket Challenge Funds ALS Clinical Trials

Rare Disease PMD Clinical Trials