Sickle Cell Disease
7 videos · updated daily
50:58 Sickle Cell: Clinical Trials Discussion at Patient Day
Suzy Lowi, Senior Clinical Research Practitioner in the Non-Malignant Haematology Clinical Trials Unit at Imperial College Healthcare NHS Trust, presents and discusses clinical trials at a sickle cell patient day run with the NIHR.
33:57 Sickle Cell Gene Therapy and Trials: Patient Session
Suzi Lowi, a clinical trials research nurse at Imperial College Healthcare NHS Trust, explains what is involved in gene therapy at a West London HCC sickle cell patient event, with audience questions.
18:21 BeTheMatch Looks at Clinical Trials for Sickle Cell
Certified genetic counselor Anne DeSalvo walks through clinical trials for sickle cell disease, patient rights and what to know before exploring a trial, for NMDP's Be The Match.
3:07 Clinical Trial Process for Sickle Cell Gene Therapy
Nicole Farmer, M.D., Staff Scientist at the NIH Clinical Center, explains the steps of the clinical trial process for sickle cell disease gene therapy, for the National Human Genome Research Institute.
2:22 RUBY Trial of EDIT-301 in Sickle Cell Disease
Rabi Hanna, MD, of Cleveland Clinic Children's gives an update on the RUBY trial of a single dose of EDIT-301, a gene editing cell therapy that modifies a patient's own stem cells, in sickle cell disease.
1:20:59 How to Achieve Patient-Centric Clinical Trials
Lance Archer, Alice Kuaban and Terry Hawrysh discuss collaborating with the patient community, applying DEI principles to planning and running trials, and strategies for patient-centric clinical trials, in a Sickle Cell Awareness Group of Ontario plenary.
1:39:16 Global Access to Sickle Cell Clinical Trials
A Sickle Cell Disease Coalition webinar in which researchers from Australia, Oman, East and West Africa, France, Brazil, the Caribbean and the NHLBI discuss sickle cell clinical trials and barriers to accessing research around the world.