Huntington's Disease
9 videos · updated daily
23:36 Gene Therapy for Huntington's Disease
Prof Sarah Tabrizi of University College London speaks on gene therapy for Huntington's disease at the Oxford-Harrington Rare Disease Centre Symposium 2026 in Oxford.
22:15 Delivering Advanced Neurotherapy Trials
Professor Liam Gray, director of the BRAIN Unit, and Professor Anne Rosser of Cardiff University discuss delivering trials of gene, RNA and cell therapies for Huntington's and Parkinson's diseases, for the Centre for Trials Research.
26:24 INVEST-HD Trial Update: Novartis Webinar
Beth Borowsky, Senior Global Programme Clinical Head in Neuroscience at Novartis, and INVEST-HD principal investigator Åsa Petersén, MD, PhD, of Lund University share updates on the INVEST-HD trial timeline in a European Huntington Association webinar.
29:23 SKY-0515 Phase 1 Results in Huntington's Disease
Skyhawk Therapeutics presents an overview of SKY-0515 and its Phase 1 clinical trial results in Huntington's disease, in a Huntington Society of Canada research webinar.
6:16 BBC News on Huntington's Disease
BBC News reports the first successful treatment of Huntington's disease, an inherited condition that kills brain cells and resembles a combination of dementia, Parkinson's and motor neurone disease. The treatment is a form of gene therapy.
53:39 Prilenia's EMA Filing for Pridopidine
Henk Shuring, Prilenia's Chief Regulatory and Commercialization Officer, explains for the European Huntington Association the March 2024 decision to seek EMA approval of pridopidine, with Prof. Anne Rosser of Cardiff University on what it means for patients.
4:49 PTC Therapeutics' Huntington's Results Explained
Astri Arnesen and Dina de Sousa of the European Huntington Association walk through the main results in PTC Therapeutics' May 5, 2025 press release and what they mean for the Huntington's disease community.
59:23 Huntington's Disease Research Update
At the Huntington's Disease Association 2025 conference, Professor Ed Wild of the National Hospital for Neurology and Neurosurgery gives a research update on current Huntington's disease trials, including the uniQure news and tominersen.
53:10 Lessons from the VIBRANT-HD Trial of Branaplam
The European Huntington Association and Novartis discuss lessons learned from the VIBRANT-HD study of branaplam, with investigator Bernhart Landwehrmeyer and Novartis's Dr. Harry Ramos and Dr. Beth Borowsky.