Cystic Fibrosis
9 videos · last 6 months shuffled daily, then older videos newest first
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1:02:09 Cystic Fibrosis State of the Science: Emily's Entourage
Emily's Entourage's scientific team reviews the research and drug development landscape for the final 10% of people with cystic fibrosis who do not benefit from mutation-targeted therapies, and presents its new Research Roadmap.
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59:06 Community Update: Infection Research
Rebekah Dedrick, PhD, Stacy Martiniano, MD, and David Nichols, MD on phage therapy and difficult-to-treat bacteria in cystic fibrosis, moderated by Sammi Marino, who has CF and has been treated for a mycobacterial lung infection.
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59:30 Kaftrio and the CFTR Modulator Trials in Cystic Fibrosis
Dr Ian Balfour-Lynn, consultant in paediatric respiratory medicine at the Royal Brompton Hospital, reviews the clinical trials that led to licensing of CFTR modulators such as Kaftrio and real-world experience with them, for the Genomics Education Programme.
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4:26 Cystic Fibrosis Trials: A Coordinator's Perspective
Julie Sweet, a Clinical Research Coordinator at the Vermont Lung Center, answers common questions about taking part in cystic fibrosis clinical research, for the Boomer Esiason Foundation.
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59:57 Research Overview: Genetic Therapies in Cystic Fibrosis
Kara Foshay, PhD, and Katie Howe, MS, CCRC, of the Cystic Fibrosis Foundation explain RNA, gene editing and gene replacement therapies for CF, how they are developed and what their clinical trials look like.
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59:26 Informed Consent and How Your Safety Is a Priority
A Cystic Fibrosis Foundation town hall from the Southeast Research Collaborative explains how safety and privacy are protected in trials and what the informed consent process involves.
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3:23 Cystic Fibrosis Trials: A Participant's Perspective
DeAnna Laramie, a patient advocate living with cystic fibrosis and a clinical trial participant, answers common questions about what taking part in clinical research is like, for the Boomer Esiason Foundation.
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3:32 Cystic Fibrosis Trials: An Investigator's Perspective
Charlotte Teneback, MD, Principal Investigator at the Vermont Lung Center, answers common questions about taking part in cystic fibrosis clinical research, for the Boomer Esiason Foundation.
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2:38 Unique Insights from Observational Clinical Trial of Kaftrio for Cystic Fibrosis
A video from the Cystic Fibrosis Trust discusses the RECOVER clinical trial for cystic fibrosis. The RECOVER trial will test a triple combination CFTR modulator compound, Kaftrio ® in people with cystic fibrosis.